Global Perspectives on Cystic Fibrosis: Trials, Therapies, and the Road Ahead

In this third and final deep-dive episode, Nicholas Simmonds highlights the importance of collaborative networks, such as the European Cystic Fibrosis Society (ECFS) Clinical Trials Network, in enabling global clinical trials. He also emphasises the central role of the patient voice in developing new therapies, using CFTR modulators as a key example.

Timestamps:

00:00 – Introduction

00:55 – ECFS Network

03:29 – Trial design

04:54 – Therapy frontiers

07:48 – Curative approaches

13:07 – Clinician message